Two Grants Awarded to Medical College of Wisconsin Researcher
July 11th 2016Researchers discovered a clinically translatable gene therapy protocol, which is a gene delivery system that introduced the production of therapeutic clotting proteins in platelets, so that the inhibition of inactivating antibodies is avoided.
FDA Approval Updates for Hemophilia Drugs
July 11th 2016Over the past few months, the Food and Drug Administration (FDA) approved several drugs for the control and prevention of bleeding episodes in patients with hemophilia. Other drug classifications granted included Orphan Drug Status and Breakthrough Therapy designation.
Analysis of Hemophilia Studies Fit Guidelines and Recommendations
July 11th 2016An analysis of randomized controlled trials (RCTs) published by the Institute for Quality and Efficiency in Health Care (IQWiG) determined that prophylactic treatment for hemophilia A is superior to on demand treatment in some outcomes.