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NORD's Voice of the Community
Latest from NORD's Voice of the Community
Dipanjan Basu, PhD, Highlights Potential of Omipalisib for Neurocutaneous Melanocytosis
January 11, 2019
Article
Dipanjan Basu, PhD, is testing non-melanoma drugs, like the investigational therapy omipalisib (GSK2126458) in cultured patient cells.
Top 5 Rare Disease News of the Week—October 14, 2018
October 20, 2018
Article
Stay up-to-date on the latest rare disease news by reading the top 5 articles of the week.
Genetic Testing for Rare Diseases with Geneticist, Debra Regier, MD
September 01, 2018
Article
In a recent webinar, geneticist Debra Regier, MD, provides an overview of the importance of genetic testing in the rare disease space.
FDA Grants Fast Track Designation to Betalutin for Follicular Lymphoma
June 12, 2018
Article
e FDA grants Fast Track designation to 177Lu-lilotomab satetraxetan (Betalutin) for the treatment of patients with relapsed/refractory follicular lymphoma after at least 2 prior systemic therapies.
"Right to Try" Bill Heads to President Trump for Approval
May 24, 2018
Article
Congress has voted to pass the Right to Try bill which will provide terminally ill patients with the ability to seek out experimental therapies not yet approved by the FDA.
NORD: The Voice of the Community - May 2018
May 21, 2018
Article
NORD's Voice of the Community - May 2018