Catch up on the hematology news and data you missed from April 2026.
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April 2026 brought major developments in hematology, particularly in sickle cell disease (SCD), with advances spanning phase 3 therapeutics, gene-editing strategies, pediatric thrombosis prevention, and global disparities research.
From promising efficacy data for etavopivat and renizgamglogene autogedtemcel (reni-cel) to new anticoagulant prophylaxis guidance for pediatric venous thromboembolism (VTE), the month’s headlines highlighted both...
Approval is based on 36-week data from BRAVE-AA-PEDS, in which 42% of patients on the 4 mg dose achieved a SALT score of 20 or less, compared with 5% on placebo.
The FDA approved once-daily oral zilurgisertib for FOP in patients aged 12 years and older after the phase 2 PROGRESS trial showed reduced new heterotopic ossification vs placebo.
As the FDA weighs its first psychedelic approval, Sarah Norman, MPP, says training, credentialing, and reimbursement are lagging while patients are already asking.
Andrea Murina, MD, weighs whether she would recommend medicine to her own children amid AI, physician burnout, and evolving residency training standards.