
Results from a phase 1-2, dose escalation study cof a single peripheral infusion of AAV5-hFVIII-SQ in 9 men with severe hemophilia A displayed that changes in the vector and gene resulted in successful gene transfer.


Results from a phase 1-2, dose escalation study cof a single peripheral infusion of AAV5-hFVIII-SQ in 9 men with severe hemophilia A displayed that changes in the vector and gene resulted in successful gene transfer.

The U.S. FDA has accepted for review the New Drug Application for Azedra (iobenguane I 131) to be indicated for patients with malignant, recurrent and/or unresectable pheochromocytoma and paraganglioma.