News

Ticagrelor 60 mg and 90 mg tablets have been indicated for lowering the risk of heart attack, or death from heart attack or stroke in patients with acute coronary syndrome.

The FDA has granted a fast track designation to FCX-013, a gene therapy for the treatment of patients with moderate to severe localized scleroderma.

A recent study found the costs of medical, laser, and surgical interventions were 2.5% or more of the median annual household income for many patients worldwide.

Study of abrupt versus gradual reduction of nicotine informs FDA-proposed rule on reducing cigarette nicotine to "minimally addictive" levels.

Implementation of antimicrobial stewardship programs in outpatient dialysis centers reduce infections caused by multidrug-resistant organisms, including Clostridium difficile.

The FDA has granted a tentative approval to Aquestive Therapeutics, Inc.’s clobazam (Sympazan) oral film for the adjunctive treatment of seizures associated with Lennox-Gastaut Syndrome (LGS) in patients 2 years of age or older.

The latest approach to developing a gene therapy for Duchenne muscular dystrophy shows promising results.

More than 2 million US outpatient visits and 3 million emergency department visits from 2005-2009 were accounted to children seeking care for mild TBI. Until now, no evidence-based clinical guidelines for pediatric mild TBI existed.

The FDA has granted a priority review for an anti-PD-1 therapy for the treatment of adults and pediatric patients with recurrent locally advanced or metastatic Merkel cell carcinoma.

The treatment may be most appropriate for toddlers who are admitted to the hospital, have severe allergies, or are seen in the emergency department.

Ibudilast has been found to slow down brain atrophy in patients with progressive multiple sclerosis.

Findings from a recent study reinforce that efforts to help patients connect with other patients should be considered a vital and beneficial element in patient management.

The principles included new and updated evidence over recent years in the field of diabetes self-management, education, and support, as well as shared decision-making skills and individualized care for patients.

The results of a recent study revealed that the implementation of a comprehensive care plan for acute exacerbations of chronic obstructive pulmonary disease (AECOPD) can be successful in reducing both readmission and mortality rates.

Stay up-to-date on the latest rare disease news by checking out our top 5 articles of the week.

The heart rhythm specialist with the UVA Advanced Imaging group discussed his team's early successes with Medtronic's heart ablation vest.

In a recent webinar, geneticist Debra Regier, MD, provides an overview of the importance of genetic testing in the rare disease space.

The results of a recent study indicate that combination DAA regimens that include sofosbuvir are effective for achieving SVR in patients with chronic hepatitis C virus and compensated liver cirrhosis.

Investigators found associations between ART and ISTI-based regimens and increased viral suppression rates across the United States.

Mechanisms underlying the disease pathology of Alexander disease, a rare leukodystrophy affecting the nervous system, have been uncovered by City of Hope investigators.

Among patients who were lost to follow-up over a year, just 7.4% attended a follow-up visit after the observed 12 months. In the total loss to follow-up patient population, they reported a mean 7.8 injection treatments and 8.5 clinic visits. In patients not lost, they reported a mean 14.3 injections and 17.1 visits.

New recommendations from the CDC's Advisory Committee on Immunization Practices reveal that health care providers have the intranasally-administered live attenuated influenza vaccine (LAIV) among their arsenal of available vaccines for the 2018-2019 flu season.

In order to successfully treat Rett syndrome, studies need to focus on a holistic approach encompassing each of the associated emotional, behavioral, and autonomic dysregulation symptoms.

DELSTRIGO and PIFELTRO have been indicated for the treatment of HIV-1 infection in adult patients with no prior antiretroviral treatment experience.

A new study has found that, based on the complexities of the EHR system they're required to use, physicians have a nearly equal chance of shortening or extending their career.

15 years ago, the Los Angeles-based educator and public health professional introduced Canary Health with his son. Here’s how the father-son team improved diabetes management online.

Harvard Medical School investigators have discovered a molecular link between aging and a genetic cause of amyotrophic lateral sclerosis and frontotemporal dementia.

In a phase 2/3 trial, the Bayer Pharmaceuticals therapy demonstrated protection from bleeding and patient safety for up to a median of 1.9 years.