News

Almost 20% of young people with autism spectrum disorder (ASD) also were diagnosed with depression in a study that tracked participants into their 20s.

A new study is the first to identify eosinophil counts as a predictor of outcomes in human patients.

Physicians are primarily delivering disease management, rather than healing and care. The current system is a placing a strain on the practice.

Investigators reported an overall mean estimation error ranging from 3.47% to 5.29% in five-year outcomes for patients with AMD.

Stay up-to-date on the latest rare disease news by checking out our top 5 articles of the week.

BioLyte Laboratories is voluntarily recalling lots of their topical gel at risk of possible microbial contamination can result in increased infections that may require medical intervention and could be potentially life threatening to certain individuals.

The FDA approved the Teva Pharmaceutical drug, just months after its phase 3 program for headache clusters was discontinued.

The National Institutes of Health has launched the Cure Sickle Cell Initiative to accelerate the pace at which genetic-based curative therapies are developed for sickle cell disease.

The device is a balloon catheter designed to treat rare, but life-threatening perforations in the coronary artery, which can occur during Percutaneous Coronary Intervention procedures.

Investigators found that active choice intervention correlated with a nearly 10% increased likelihood of patients receiving the seasonal flu vaccine.

Patients with asthma and eosinophilia have thicker airway nerves, according to new research.

Addressing housing arrangements during a medical visit may be as important as addressing blood pressure or blood sugar levels.

Moxetumomab pasudotox (Lumoxiti, AstraZeneca)is approved for adults with relapsed or refractory HCL who received at least 2 prior systemic therapies, including treatment with a purine nucleoside analog.

The FDA has approved the subcutaneous formulation of tocilizumab (Actemra) for the treatment of active systemic juvenile idiopathic arthritis in patients two years of age and older.

Novartis reported that 59% of patients at 24 weeks experienced little to no impact of their condition on their quality of life. Additionally, 87% of bio-naïve psoriasis patients remained on secukinumab through 12 months, indicating its tolerability in real-world settings.

The FDA has granted an orphan drug designation to Syntimmune Inc.’s SYNT001 for the treatment of pemphigus.

The acceptance comes less than a month since the FDA had approved the anti-VEGF therapy for the treatment of wet AMD. Its mechanism of action allows it to block new blood vessel growth and the passing of fluids through blood vessels in the eye.

A new meta-analysis aimed to quantify the effect, if any, of physician burnout on patient wellbeing. They found the links are strong and consequential.

Data presented at the2018 World Congress on Parkinson's Disease and Related Disorders indicate that valbenazine is a promising treatment for tardive dyskinesia, while opicapone may be a new effective treatment for Parkinson disease.

The FDA has granted a fast track designation to pamrevlumab for the treatment of patients with idiopathic pulmonary fibrosis (IPF).

The supplemental BLA seeks FDA approval for alirocumab (Praulent) as a treatment to reduce overall risk of major adverse cardiovascular events.

An investigative team from St. Jude Children’s Research Hospital have identified weaknesses to target in rhabdomyosarcoma, leading to a promising precision medicine treatment that has already hit clinical trials.

After 10 days of transcranial magnetic stimulation, patients reported significant decreases in withdrawal symptoms like craving, quality of sleep, and mood status.

The combination of montelukast and budesonide was found more effective than budesonide alone in children with chronic cough-variant asthma in a China retrospective study.

A study of primary care patients found that of patients screened for alcohol use, just 2.4% were also screened for depression. Men and racial/ethnic minorities were less likely to be screened for depression.

A daily dose of aspirin could reduce HIV transmission rates by reducing inflammation and thus the number of HIV target cells in the female genital tract.

The FDA has granted a fast track designation to Immune Pharmaceuticals, Inc.’s bertilimumab for the treatment of bullous pemphigoid.

New research says it’s medically possible to use HCV-positive patients as liver donors. Now, a new study finds it’s also cost-effective.